The Rett Syndrome Research Trust (RSRT) is the patient advocacy ...
As the largest funder of Rett syndrome research worldwide, RSRT has played a vital role in initiating and evolving the trajectory of progress toward cures. All genetic medicines in development by biopharma have leveraged discoveries and resources made possible by RSRT.
About RSRT - Rett Syndrome Research Trust
We are relentless in our dedication to advancing the research to a cure for Rett Syndrome. See a bit of our history and meet the people here at RSRT.
RSRT | Roadmap to Cures: Non-Viral Delivery - Rett Syndrome …
In 2007, Prof. Adrian Bird shocked the scientific and Rett community by showing that Rett symptoms in mice models disappeared upon restoration of MECP2. Within months Monica launched RSRT, with Prof. Bird at her side, with the sole purpose of accelerating cures. Explore our journey so far.
RSRT launches program to advance genetic therapies for Rett
Jun 12, 2024 · RSRT launched Roadmap to Cures in 2017 to advance genetic medicine approaches targeting the root cause of Rett. The organization has invested more than $11 million in two gene therapy programs for Rett that are now in clinical trials: Neurogene’s NGN-401 and Taysha Gene Therapies’ TSHA-102.
RSRT Invests Over $3M in Research Toward Finding a Cure for Rett
Jan 28, 2022 · For one of the research projects, RSRT is investing more than $1 million into work that seeks to reactivate the MECP2 gene. Rett is mostly caused by mutations in the MECP2 gene, which is located on the sex-determining X chromosome.
Rett Syndrome Research Trust Launches Roadmap to Cures to
Jun 5, 2024 · RSRT’s new MECP2 Editing Consortium is a critical component of Roadmap to Cures. The Consortium is a collaboration among six labs, aimed at creating DNA and RNA editing therapies for Rett...
Rett Syndrome Research Trust - National Organization for Rare Disorders
The Rett Syndrome Research Trust (RSRT) is the organization working to cure Rett syndrome. As the largest funder of Rett syndrome research worldwide, RSRT has played a vital role in initiating and evolving the trajectory of progress toward a cure.
Touchless Emerald AI biosensor gets $1.1M funding boost from RSRT
Mar 1, 2023 · The Rett Syndrome Research Trust (RSRT) has granted $1.1 million to help advance the development of the Emerald biosensor to accurately assess symptoms of Rett syndrome.
RSRT: Where We've Been - Rett Syndrome Research Trust
Since the moment RSRT was created, we’ve been optimistic about curing Rett. Fueling our optimism are three key facts: a single gene means we have a clear target, Rett brain cells don’t die, and restoring levels of MECP2 reverses symptoms in mice models.
Research. Family Support. Advocacy. | International Rett Syndrome ...
IRSF is the leading research, family support, and advocacy organization for Rett syndrome, transforming lives every day in our fight to treat and cure the disorder.