A second case of acute liver failure resulting in death has been reported in nonambulatory DMD patients treated with Elevidys.

Dog exposure was linked to significant changes in some genetic factors associated with risk for atopic eczema.

In the first half of 2025, eight systems have performed first-of-their-kind procedures and clinical treatments. 1. Morgantown, W.Va.-based WVU Heart and Vascular Institute physicians completed the ...

Former Florida Times-Union sports columnist Gene Frenette joined senior writer John Oehser for this 2025 offseason O-Zone ...

Sarepta Therapeutics Inc. plummeted in early trading after reporting a second patient died of acute liver failure while being treated with its gene therapy for a rare muscle disorder.

Supernus Pharmaceuticals said it is acquiring Sage Therapeutics, the distressed maker of a drug for postpartum depression, ...

Another person treated with Elevidys suffered acute liver failure, leading Sarepta to discontinue treatment in certain patients while it evaluates new safety precautions.

Ocugen has announced the US Food and Drug Administration (FDA) has cleared the Investigational New Drug (IND) amendment to ...

Gucci Owner Picks Auto Executive for One of Global Luxury's Top Jobs Francois-Henri Pinault is stepping back as CEO of Kering, hoping Luca de Meo can pull Gucci and Saint Laurent out of a slump.

Scientists at UCLA and the University of Toronto have developed an advanced computational tool, called moPepGen, that helps identify previously invisible genetic mutations in proteins, unlocking new ...

In today's Pharmalittle roundup, we're reading about a Sarepta setback with its Duchenne drug, the FDA workload causing a ...

Researchers discovered a previously unknown function of RNA, potentially opening the door to new ways to treat cancer and ...