UCLA Health researchers say study findings uncover Huntington's disease mechanisms and pave new ways to develop treatments.

In one tiny town, more than a dozen people were diagnosed with the rare neurodegenerative disease ALS. Why? I n March 2009, ...

Why didn’t analysts share the same fear that gripped investors about Sarepta stock? One reason is the known risk of acute liver injury associated with adeno-associated virus vector (AAV)-based gene ...

Sarepta Therapeutics (NASDAQ:SRPT – Free Report) had its target price lowered by Scotiabank from $105.00 to $80.00 in a ...

MD-PhD student Tomer Kagan and Dr. Tal Laviv. A novel scientific method developed at Tel Aviv University promises to ...

Treatment shows potential to slow the progression of human degenerative eye diseases, including retinitis pigmentosa.

An experimental treatment appears to delay Alzheimer's symptoms in some people genetically destined to get the disease in ...