Combined organ-specific mRNA and lipid nanoparticle therapy could repair damaged lungs
A combination of mRNA and a new lipid nanoparticle could help heal damaged lungs, according to new research from the Perelman ...
Packing lipid nanoparticles with tumor proteins to boost cancer vaccine potency
The concept of using vaccines to treat cancers has been around for several decades. A vaccine was first approved for prostate cancer in 2010, and another was approved in 2015 for melanoma. Since then, ...
FDA Approves Mirum Pharmaceuticals Treatment for Lipid-Storage Disease
The Food and Drug Administration approved Mirum Pharmaceuticals' Ctexli to treat Cerebrotendinous Xanthoma, a very rare lipid-storage disease. The approval makes Ctexli, or chenopod, the first ...
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FDA ap­proves first drug to treat ul­tra-rare lipid stor­age dis­ease
The FDA on Friday approved Mirum Pharmaceuticals' Ctexli to treat adults with cerebrotendinous xanthomatosis (CTX), a rare, progressive and genetic disease.