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Why Sarepta Therapeutics (SRPT) Shares Are Sliding Today
What Happened? Shares of biotech company Sarepta Therapeutics (NASDAQ:SRPT) fell 24.9% in the pre-market session after the ...
Sarepta's stock slammed after patient dies of liver failure. Here's what Wall Street is saying.
Sarepta Therapeutics Inc.'s stock tumbled 23% on Tuesday after the biotech said a patient who used its gene therapy Elevidys for the rare disease Duchenne muscular dystrophy has died of acute liver ...
Patient dies following muscular dystrophy gene therapy, Sarepta reports
A patient has died while taking a closely watched gene therapy for muscular dystrophy. Sarepta Therapeutics announced the ...
MarketWatch14d
Capricor Therapeutics' Cell Therapy for Muscular Dystrophy Patients to Get FDA Priority Review
The Food and Drug Administration has accepted Capricor Therapeutics' application seeking approval of its cell therapy deramiocel for muscular dystrophy patients and granted it a priority review.
The Guardian Nigeria19d
Group warns against locking up children with muscular dystrophy, rare diseases
Aside from muscular dystrophy, other examples of rare diseases include hemophilia, an inherited blood disorder that causes excessive bleeding and bruising; phenylketonuria, an inherited disorder ...
Muscular Dystrophy News19d
Steve Bryson, PhD, science writer—
Preventive treatment with standard heart medications — when given before the onset of cardiac troubles — extends survival among males with Duchenne muscular dystrophy (DMD), according to data from the ...
Hindustan Times20d
South Korean student with paralysis and muscular dystrophy earns master’s degree using just eye blinks
Jang Ik-sun, a 37-year-old student from South Korea, has achieved an extraordinary academic milestone despite living with muscular dystrophy, a condition that has left him almost entirely ...
Phys.org21d
Nanoparticles deliver microRNAs to muscle stem cells for potential muscular dystrophy treatment
Get Instant Summarized Text (Gist) Nanoparticles have been developed to deliver microRNAs to muscle stem cells, offering a potential treatment for Duchenne muscular dystrophy. These nanoparticles ...
Medical Xpress21d
Gene therapy can improve vision in young children with AIPL1-associated retinal dystrophy
This is the first human trial of gene supplementation therapy targeting this condition. Retinal dystrophy caused by biallelic variants in the AIPL1 gene leads to severe visual impairment from ...
MarketWatch22d
Entrada Shares Climb After FDA Removes Hold on Muscular Dystrophy Treatment
Shares of Entrada Therapeutics rose after regulators removed a clinical hold and said its lead product candidate could be studied as a treatment for Duchenne muscular dystrophy. The stock was up 9 ...
Business Wire22d
Precision BioSciences Announces Oral Presentation at the 2025 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
today announced that the company will present preclinical data from the PBGENE-DMD program for the treatment of Duchenne muscular dystrophy (DMD) during an oral presentation at the 2025 Muscular ...