Harvard Medical School9h
Creating the World’s First CRISPR Medicine, for Sickle Cell Disease
In December 2023, through the development efforts of CRISPR Therapeutics and Vertex Pharmaceuticals, their decades-long ...
High-cost sickle cell gene therapies push insurers and Medicaid programs to find new payment models
The high cost of sickle cell gene therapies is pushing private insurers and Medicaid programs to develop new payment models.
Fulcrum: Next Set Of SCD Data Is Crucial For Continued Pipeline Advancement
Fulcrum Therapeutics' promising treatment for Sickle Cell Disease and their strong financial position, despite setbacks.
MUSC expands gene therapy, resources for Sickle Cell ‘warriors’ in South Carolina
The Medical University of South Carolina is expanding its access to state-supported Sickle Cell programs for “warriors,” or ...
The Scientist1y
Handmade Hemoglobin, 1912-2012
Today, the cause of sickle cell disease is well understood to be a point mutation ... test to detect sickle hemoglobin by triggering temperature-mediated, reversible polymerization, and he was ...