Sickle Cell Disease (SCD) is a genetic blood disorder that primarily affects individuals of African descent, leading to various health complications and a significant burden on healthcare systems.

Given the remarkable advances seen with gene therapies for sickle cell disease (SCD), it may ... as cutting-edge therapies face a long journey to treat patients at scale, the community recently ...

Children with moyamoya syndrome (including those with sickle cell disease) should be referred for evaluation to a center with expertise in evaluating patients for surgical revascularization (B).