The U.S. FDA has granted orphan drug designation for Eli Lilly's olomorasib for treatment of KRAS G12C-mutant non-small cell ...

A Bitter Battle Over the ‘Orphan Drug’ Program Leaves Patients’ Pocketbooks at Risk. By Sarah Jane Tribble February 22, 2023 . Patients who depend upon special drugs to treat rare diseases are caught ...

The U.S. Food and Drug Administration (FDA) has granted Orphan Drug Designation to GENFIT’s (NASDAQ: GNFT) drug candidate GNS5611 (ezurpimtrostat) for the treatment of cholangiocarcinoma.

Tempest Therapeutics TPST announced that the European Medicines Agency (EMA) has granted an orphan drug designation (ODD) to its oral PPAR-alpha antagonist, amezalpat (TPST-1120), for the treatment of ...