A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

Victoria Gray is the first person in the world to receive CRISPR,  a gene-editing therapy for sickle cell disease created by ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

Mariam Mohammed says her younger son died when she could not get treatment for him at a U.S.-funded clinic that had ...

The Pediatric Emergency Medicine and Pediatric Hematology/Oncology divisions at the Medical University of South Carolina ...