Niemann-Pick disease affects multiple systems throughout the body. It has many symptoms, and the severity varies from case to case. Rather than being one disease, Niemann-Pick has four distinct types.

Niemann-Pick disease is a rare genetic medical condition. There are four variants of this disease, categorized as type A, type B, type C, and type D. Niemann-Pick disease causes a variety of ...

When a 17-year-old Minnesota boy got sick with a mysterious illness, his mom went on a quest for answers. Connor Martin, of ...

In the space of four days, the number of FDA-approved therapies for ultra-rare genetic disorder Niemann-Pick disease has gone from zero to two, transforming the prospects for patients. IntraBio's ...

Zevra Therapeutics' Miplyffa has become the first medicine to be approved by the FDA for the ultra-rare genetic disorder Niemann-Pick disease. The US regulator has cleared Miplyffa (arimoclomol ...

After LIV Miami in two weeks, it’s the Masters. Niemann will make his sixth start there and has yet to finish in the top 10, but he’s been a trendy sleeper pick for the last couple of years. He’s ...

This recommendation is not intended to affect treatment with olipudase alfa that was started in the NHS before this guidance was published. People having treatment outside this recommendation may ...

One of the more obvious moves for the Los Angeles Chargers going into free agency, it seemed, was bringing back linebacker Nick Niemann. Or not—the Houston Texans had other plans. According ...

The Texans are signing linebacker Nick Niemann to a two-year deal with a max value of $6.5 million, Tom Pelissero of NFL Media reports. The Chargers made Niemann a sixth-round pick in 2021, and he ...