News

Fierce Biotech20h
Gene editing leaders call for 10-year suspension of heritable human genome editing
An international group of gene editing leaders has put out a call for a 10-year ban on heritable human genome editing (HHGE), ...
Taysha Gene Therapies, Inc. (TSHA)’s TSHA-102 Shows Promising Results in Rett Syndrome Patients Aged 6+
Taysha Gene Therapies, Inc. (NASDAQ: TSHA) has announced pivotal progress in its TSHA-102 gene therapy program for Rett ...
Study reveals novel strategy for in vivo blood stem cell gene therapy
A team of scientists from the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget) in Milan, Italy, has identified a ...
News-Medical.Net on MSN13h
Scientists identify early life opportunity for in vivo stem cell gene therapy
A team of scientists from the San Raffaele-Telethon Institute for Gene Therapy (SR-Tiget) in Milan, Italy, has identified a ...
uniQure's AMT-130 Gene Therapy Warrants An Upgrade
Qure divested for $25M, advanced AMT-130 with FDA approvals, and building infrastructure. A strong balance sheet backs ...
Could gene therapy end thalassemia? China's breakthrough sparks hope
With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...
Science Daily4d
Gene Therapy News
Infant With Rare, Incurable Disease Is First to Successfully Receive Personalized Gene Therapy Treatment May 15, 2025 — A research team has developed and safely delivered a personalized gene ...
Science News16h
Personalized gene editing saved a baby, but the tech’s future is uncertain
The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.