By Gina Kolata Gina Kolata has reported on gene therapy for nearly 30 years and on sickle cell disease since 2018. A panel of experts said on Tuesday that a groundbreaking treatment for sickle ...

Almost four years ago, Gray became one of the first patients with a genetic disorder — and the first patient with sickle cell disease — to get an experimental treatment that uses the ...

Four years ago, Victoria Gray was lying in a hospital bed, exhausted by a lifetime with sickle cell disease and recovering from a grueling experimental treatment she hoped would save her.

The Food and Drug Administration on Friday approved two gene therapies to treat sickle cell disease, one of the which is the first CRISPR/Cas9-based treatment to win regulatory approval in the US.

Called Casgevy, the treatment is intended to cure sickle-cell disease and a related condition, beta thalassemia. The manufacturers, Vertex Pharmaceuticals, based in Boston, and CRISPR Therapeutics ...

He’s got new blood. A Long Island hospital said it administered life-changing Lyfgenia gene therapy treatment and successfully wiped away sickle cell disease from a Laurelton man. Cohen Children ...

He had come to Florida to surprise his sister for her birthday. But instead, he had become so weak from sickle cell anemia that he had to be carried into a local hospital, then sent to another ...

A patient on Long Island is the first in New York to be cured of sickle cell anemia, doctors say. They credit state-of-the-art genetic treatment. Medical history made at Cohen Children's Medical ...

The sudden death of 16-year-old Central Dauphin student Justin Johnson after being chased by other students from his school could have been connected to the boy’s sickle cell disease ...