HSCT may be a suitable treatment for X-linked ALD adults with early signs of cerebral involvement. Very long-chain fatty acid levels and adrenoleukodystrophy protein (ALDP)-deficiency are strongly ...

X-ALD is characterized by a breakdown in the protective barriers surrounding brain and nerve cells that cause a buildup of ...

Kyrie has what’s known as Childhood Cerebral ALD. He’s been receiving treatment in Minneapolis, Minnesota. In January he had a cord blood transplant, and his family hopes to welcome him back ...

Alan Alda, 89, makes a lovely appearance in Tina Fey's Netflix series "The Four Seasons," which is adapted from his 1981 ...

Around 40% of patients develop the cerebral form of ALD, which in turn affects around one in 17,000 live births. A few weeks ago, Bluebird reported new data from the phase 2/3 STARBEAM trial of ...

One of the unexplored frontiers in ALD is the enhancement of ALD reactions using non-thermal methods. We are exploring the ability of low energy electrons to enhance ALD reactions. The goal is to ...

Thus, the in vivo efficacy of treatment can be monitored by determination of its effect on VLCFA levels in the tissues, brain and adrenal gland, the organs most affected in X-ALD. 4PBA corrects ...